Gene therapy for muscular dystrophy using AAV

January 16, 2018 - 12:30pm to 1:30pm
Jeffrey S. Chamberlain, Ph.D.

The University Program in Genetics and Genomics (UPGG) Presents Tuesday Seminar Series
Host: Dwight Koeberl

Dr. Chamberlain is at the University of Washington, School of Medicine, Department of Neurology.

His group is focused on developing treatments for the muscular dystrophies. They have been using AAV vectors to deliver genes systemically to muscles, an approach that is about to enter clinical trials. 
The AAV system requires the use of compact genes and regulatory cassettes, which will be discussed.

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